Business Description
ProQR Therapeutics is a Dutch biotech company working to develop new treatments for genetic diseases that currently have few or no options. Its core focus is RNA editing, using its Axiomer technology to correct faulty genetic instructions without permanently altering DNA. The company has several treatments in development targeting conditions such as Rett syndrome, liver disease, and cardiovascular disorders. ProQR also works alongside Eli Lilly to discover and bring to market new medicines for genetic conditions affecting the liver and nervous system.
